One-year safety and efficacy of mitapivat in sickle cell disease: follow-up results of a phase 2, open-label study
Description
Targeting the primary pathogenic event of sickle cell disease (SCD), polymerization of sickle hemoglobin (HbS), may prevent downstream clinical events. Mitapivat, an oral pyruvate kinase (PK) activator, has therapeutic potential by increasing
